Precision gene editing could prevent vision loss from Stargardt disease
Researchers have developed a therapy to treat Stargardt disease, the most common form of inherited macular degeneration, ...
Breakthrough Gene Editing Technique Offers Hope for Stargardt Disease Patients
Researchers have developed a highly efficient gene editing therapy that could potentially treat Stargardt disease, the most common form of ...
AZoLifeSciences on MSN4d
New Gene Editing Therapy Shows Promise for Treating Stargardt Disease
Researchers have developed a highly efficient gene editing therapy that could potentially treat Stargardt disease, the most ...
GEN5d
Base Editing Addresses Inherited Macular Degeneration in Primate, Human Tissue Models
The adenine base editor corrected the most common mutation associated with Stargardt disease in the ABCA4 gene with no off-target effects.
Alkeus Pharmaceuticals to Present at the 43rd Annual J.P. Morgan Healthcare Conference
Alkeus’ presentation, which will include new data from the company’s TEASE-3 study of gildeuretinol in early-stage patients with Stargardt disease, will be Tuesday, January 14, at 4:30 p.m. PST at The ...