Overall, the life expectancy of patients with SCD is lower than that of persons without SCD. 1 However, life expectancy varies depending on the type of disease, treatments administered, and ...

PER has the advantage that it can be used in all patients with DEEs since it can be used regardless of the epilepsy syndrome. After 60 months of treatment with PER, the rates of patients who ...

Which of the statements below about the diagnosis of immunoglobulin G4-related disease (IgG4-RD) are correct? Select one of the options for each question, then submit your answers to see how well you ...

The differences in mast cell morphology and immunophenotype suggest the need for additional research into the role of mast cells in the liver in SM. A new study of patients with advanced systemic ...

Which of the statements below about the diagnosis of fetal and neonatal alloimmune thrombocytopenia (FNAIT) are correct? Select one of the options for each question, then submit your answers to see ...

In part 1 of its phase 2 APEX trial, nearly all patients (94%) experienced a reduction of 50% or more in serum tryptase levels. Cogent Biosciences shared promising updated results from part 1 of its ...

The patient remains in remission for both conditions after over a year of therapy, with a significantly reduced prednisolone dose. A recent case highlights the successful treatment of Takayasu ...

The study will measure adverse events, dose limiting toxicities, and laboratory test results among PiZZ and PiMZ patients with AATD after a single dose of BMN 349. A new study in the United States is ...

The patient was safely treated with dexamethasone, despite caution regarding corticosteroid use in patients with SCA. An unusual case involving a patient with sickle cell anemia (SCA), a form of ...

Until more sensitive blood tests are available, bone marrow biopsy is still the gold standard for assessing patients with suspected SM. A new study has determined that even the most sensitive tests ...

Patients with CIDP had significantly lower levels of total N-glycans in their serum compared to healthy people. The levels of sialylated N-glycans in the serum could be a novel biomarker in chronic ...

The researchers of the current analysis sought to report on updated efficacy and safety results from the fully enrolled part 1 of the phase 2 APEX trial. Among individuals with advanced systemic ...