"The addition of Jnana's drug discovery technology and small molecule pipeline in PKU and autoimmune diseases will strengthen our R&D in the Boston area of the US, one of the most important ...

such as Phenylketonuria (PKU) and Maple Syrup Urine Disease (MSUD). Group 3 covers conditions like Gaucher Disease and Pompe ...

An 11-year-old girl with the rare disease phenylketonuria (PKU) has lost a legal battle in the High Court over a decision by NICE to deny NHS access to the only approved drug in the UK.

NGGT has initiated Phase I/II clinical trials in the U.S. and China to evaluate the safety and efficacy of NGGT002 for the treatment of Phenylketonuria WALNUT CREEK, ...

The first patient dosed with NGGT002 in the IIT trial showed a persistent plasma phenylalanine level within the normal range 40 weeks after the drug was dosed. Phase I/II clinical trials in the U.S.

The patents, based on these new findings, cover additional claims for Relief’s investigational drug RLF-OD032, a highly concentrated, novel liquid formulation of sapropterin dihydrochloride, for the ...

(“Next Generation Gene Therapeutics” or “NGGT”), a clinical-stage biotechnology company pioneering the next wave of gene therapy innovation for genetic rare diseases, today announced positive new data ...

Migraine medications fall into two broad categories. When a migraine begins, you can turn to drugs that ease the pain (acute treatment). If you have recurrent or chronic migraines, you can take ...

The U.S. unit of Indian drugmaker Dr. Reddy’s Laboratories is recalling 331,590 bottles of cinacalcet tablets used to treat hyperparathyroidism due to the presence of a known carcinogen. | The U.S.

GENEVA, SWITZARLAND / ACCESSWIRE / October 29, 2024 /RELIEF THERAPEUTICS Holding SA (SIX:RLF)(OTCQB:RLFTF)(OTCQB:RLFTY) (Relief, or the Company), a biopharmaceutical company committed to delivering ...

Biologics, also called biologicals, are drugs made from living things. Sometimes, these substances come from human donors, such as donated blood. Other times, they are grown in a laboratory.

Using drugs changes a person's brain structure and functioning, particularly in areas involved in reward, stress, and self-control. These alterations make it harder for people to stop using substances ...