How can you measure a person's quality of life? For columnist Patrick Moeschen, the key is deciding for yourself what a good ...

Sevasemten significantly reduced two markers of muscle damage in treated Becker muscular dystrophy patients in Phase 2 CANYON ...

Columnist Shalom Lim appreciates how Duchenne never offers a dull moment as he prepares for the challenges and adventures in ...

FSHD exacts a toll on columnist Robin Stemple when he is out and about. He calls these symptom flares "FSHD hangovers." ...

Learning that three of her sons had DMD challenged columnist Betty Vertin, but now she embraces the highs and lows of the experience.

A woman who developed heart failure due to Duchenne muscular dystrophy (DMD) was diagnosed and treated before she got pregnant, which led to a healthy outcome for her and her baby girl, according to ...

Agamree (vamorolone) has been recommended for use in the National Health Service (NHS) in England, Wales, and Northern Ireland for treating Duchenne muscular dystrophy (DMD) patients, 4 and older. “We ...

Arrakis Therapeutics’ investigational RNA-targeted small molecule (rSM) therapies were found to work as intended in preclinical studies and eased symptoms in a mouse model of myotonic dystrophy type 1 ...