Muscular Dystrophy News6 天
Capricor now seeking FDA approval of DMD therapy deramiocel
Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...
Muscular Dystrophy News8 天
C-Path to lead new task force seeking to advance LGMD therapies
The Critical Path Institute will lead a new task force to advance the development of therapies for limb-girdle muscular ...
Muscular Dystrophy News9 天
Educating all ages about living with muscular dystrophy
Columnist Patrick Moeschen has learned to tailor his descriptions of living with limb-girdle muscular dystrophy to his ...
Muscular Dystrophy News13 天
Rare pediatric disease designation granted to LAMA2-CMD therapy
The FDA has granted rare pediatric disease designation to Modalis' MDL-101 therapy candidate for LAMA2-related congenital ...
Muscular Dystrophy News6 天
Every week, we try to organize chaos in our family of 9
What’s a typical week as a caregiver of three sons with Duchenne muscular dystrophy (DMD) like? As a primary caregiver to Max, 18, Rowen, 15, and Charlie, 13, my honest answer is that I wish I knew!
Muscular Dystrophy News23 天
Working Through the Process — Robin Stemple
Rob Stemple is a lifelong advocate for people with disabilities. He was diagnosed with FSHD in 1971 at age 14. Rob struggled with its’ affects for over 50 years. He lost his eyesight in a devastating ...