“Wicked” is the musical movie superstar of the moment. I loved “The Wizard of Oz” growing up, and while I haven’t seen the ...

Columnist Halsey Blocher, who lives with SMA, feels a sense of connection with a Christmas movie's depiction of a disabled princess.

Nearly 4 of every 5 infants in Italy born with SMA type 1 since the approval of disease-modifying therapies (DMTs) are alive, ...

Nearly 4 of every 5 infants with spinal muscular atrophy (SMA) type 1 born in Italy during the era of disease-modifying therapies (DMTs) are still alive, illustrating that such treatment has ...

Columnist Ari Anderson has set a goal for 2025: to multiply the chances of good things coming his way each time they happen.

Natalie Katz, MD, is an assistant professor of pediatrics in the division of neurology at Duke University and co-directs the Duke Children’s Neuromuscular Program, which provides comprehensive ...

Edward Smith, MD, is an adjunct professor of pediatrics at Duke University Hospital. He earned his medical degree from the University of Mississippi School of Medicine and has practiced since 2007. He ...

An algorithm may help predict the risk of scoliosis in patients who have received disease-modifying SMA treatment, a study ...