The phase 3 STEER study enrolled 127 treatment-naïve patients aged 2 to less than 18 years with SMA type 2 who were able to sit but had never walked independently.

The researchers found that between 1999 and 2022, there were 63,550,429 deaths in the United States, of which 0.06% had cold recorded as an underlying or contributing cause of death. Cold-related ...

The resubmitted NDA for sotagliflozin for adults with T1D and CKD included post hoc analyses from the TANDEM clinical development program and post hoc analysis from the SCORED trial.

Health sector's share of the economy was similar in 2023 and 2022, but lower than in 2020 and 2021, during height of COVID-19 ...

The ongoing shortage of liraglutide injection and other GLP-1 medications prompted the FDA to prioritize the generic drug applications for these medications in order to improve patient access.

(HealthDay News) — Higher daily step counts are associated with fewer depressive symptoms in adults, according to a systematic review and meta-analysis published online online December 16 in JAMA ...

According to Vertex Pharmaceuticals, approximately 300 additional people with CF are now eligible to receive treatment.

Veligrotug is an investigational monoclonal antibody that inhibits the activity of insulin-like growth factor-1 receptor.

The approval was based on data from the randomized, double-blind, placebo-controlled phase 3 URO-901-3005 trial.

Results from the VENTURE trial showed significant reductions in weight and hunger among younger patients treated with ...

Betamethasone sodium phosphate 3mg/mL; for IM, intra-articular or intralesional inj. Potentiated by CYP3A4 inhibitors (eg, ketoconazole, macrolides), cyclosporine, estrogens. Antagonized by CYP3A4 ...

The approval was based on data from the randomized, placebo-controlled, double-blind, phase 3 RATIONALE-305 trial.